Asked by Blaze Roque on Apr 28, 2024
Verified
List two sites of ex vivo gene therapy and indicate the type of therapy being conducted.
Ex Vivo Gene Therapy
A form of gene therapy where cells are modified outside the body and then re-introduced into the patient.
Sites
Locations or positions in a particular area, often used in the context of archaeological digs, web URLs, or locations for construction.
Type of Therapy
Refers to various treatments or interventions designed to alleviate symptoms, treat disease, or improve well-being.
- Describe the fundamental concepts and uses of ex vivo and in vivo gene therapy.
Verified Answer
ZK
Zybrea KnightMay 02, 2024
Final Answer :
Possible answers include:
1. Skin: gene transfer by modifying blood cells (skin cancer)
2. Liver: gene transfer by modified implants (familial hypercholesterolemia)
3. Endothelium, blood vessel lining: gene transfer by implantation of modified implants (hemophilia and diabetes mellitus)
4. Bone marrow: gene transfer by implantation of modified stem cells (SCID and sickle-cell disease)
1. Skin: gene transfer by modifying blood cells (skin cancer)
2. Liver: gene transfer by modified implants (familial hypercholesterolemia)
3. Endothelium, blood vessel lining: gene transfer by implantation of modified implants (hemophilia and diabetes mellitus)
4. Bone marrow: gene transfer by implantation of modified stem cells (SCID and sickle-cell disease)
Learning Objectives
- Describe the fundamental concepts and uses of ex vivo and in vivo gene therapy.